Hematopoietic stem-cell gene therapy is associated with restored white matter microvascular function in cerebral adrenoleukodystrophy

Arne Lauer(Goethe University Frankfurt), Patricia L. Musolino(Harvard University), Kyrre E. Emblem(Oslo University Hospital), David Rohde(Harvard University), Florian Eichler(Harvard University), Jayashree Kalpathy–Cramer(University of Colorado Denver), Vijai Krishnan(Massachusetts General Hospital), Paul A. Caruso(Lucile Packard Children's Hospital), Myoung Soo Choi(Massachusetts General Hospital), David A. Williams(Boston Children's Hospital), Kim Mouridsen(Aarhus University), Samantha L. Speroni(Massachusetts General Hospital), Cole A. Lusk(Massachusetts General Hospital), Siobhán McCarthy(Massachusetts General Hospital), Xiao Da(Athinoula A. Martinos Center for Biomedical Imaging), Mikkel Bo Hansen(Aarhus University), Christine Duncan(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Daniel J. Loes(Inserm)
Nature Communications
April 5, 2023
Cited by 25


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