Mini-COMET study: Effects of 97 weeks of avalglucosidase alfa dosing on ptosis in participants with infantile-onset Pompe disease who were previously treated with alglucosidase alfa
Priya S. Kishnani(Duke Medical Center), S. Grace Prakalapakorn(Duke University), James Davison(Great Ormond Street Hospital for Children NHS Foundation Trust), Satoko Kumada(Tokyo Metropolitan Neurological Hospital), Swathi Tammireddy, Marguerite C. Weinert, Kristina An Haack(Sanofi (France)), Alexander Broomfield(St Mary's Hospital), Hirotaka Ohki(Tokyo Metropolitan Children's Medical Center), Tianyue Zhou, David Kronn(New York Medical College), Yin‐Hsiu Chien(National Taiwan University Hospital), Samia Pichard, Sihoun Hahn(Mayo Clinic)
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