Hematopoietic stem cell transplantation for Wiskott-Aldrich syndrome: an EBMT Inborn Errors Working Party analysis
Michael H. Albert(LMU Klinikum), Arjan C. Lankester(Leiden University Medical Center), Marina Cavazzana(Université Rennes 2), Alexey Maschan(Dmitry Rogachev National Research Center of Pediatric Hematology, Oncology and Immunology), Andrew R. Gennery(Newcastle upon Tyne Hospitals NHS Foundation Trust), Benyamin Markovitch(European Society for Blood and Marrow Transplantation), Olga Aleinikova(Stichting Kinderoncologie Nederland), Ansgar Schulz(University Hospital Ulm), Fabian Hauck(Ludwig-Maximilians-Universität München), Su Han Lum(Royal Manchester Children's Hospital), Franco Locatelli(Bambino Gesù Children's Hospital), Jacek Winiarski(Karolinska University Hospital), Alexander Kulagin(First Pavlov State Medical University of St. Petersburg), Despina Moshous(Hôpital Necker-Enfants Malades), Alain Fischer(Inserm), Felipe Suárez(Hôpital Necker-Enfants Malades), Sheree Hazelaar(European Society for Blood and Marrow Transplantation), Marco Zecca(Policlinico San Matteo Fondazione), Virginie Courteille, Barış Kuşkonmaz(Hacettepe University), Caroline A. Lindemans(University Medical Center Utrecht), Martin G. Sauer, Ivana Boďová(National Institute of Cardiovascular Diseases), Alessandro Aiuti(University of Rome Tor Vergata), Roland Meisel(Düsseldorf University Hospital), Alphan Küpesiz(Akdeniz University), Tiarlan Sirait(European Society for Blood and Marrow Transplantation), Paul Veys(Great Ormond Street Hospital), Marianne Ifversen(Copenhagen University Hospital), Mary Slatter(First Pavlov State Medical University of St. Petersburg), Maria Ester Bernardo(Unknown), Tanja C. Vallée(Ludwig-Maximilians-Universität München), Dmitry Balashov(Dmitry Rogachev National Research Center of Pediatric Hematology, Oncology and Immunology), Robert Chiesa(Great Ormond Street Hospital), Katerina Bakunina(Erasmus MC Cancer Institute), Petr Sedláček(University Hospital in Motol), Christoph Klein(Ludwig-Maximilians-Universität München), Bénédicte Bruno(Centre Hospitalier Universitaire de Lille), Tayfun Güngör, Krzysztof Kałwak(Poznan University of Medical Sciences), Fulvio Porta(Ospedale dei Bambini Vittore Buzzi), Bénédicte Neven(Université Paris-Panthéon-Assas)
Cited by 85
Related Papers
<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1
|Science|2003|3.5k
Impaired type I interferon activity and inflammatory responses in severe COVID-19 patients
|Science|2020|3.2k
Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease
|Science|2000|2.6k
A Serious Adverse Event after Successful Gene Therapy for X-Linked Severe Combined Immunodeficiency
|New England Journal of Medicine|2003|1.8k