Mini-COMET: effects of avalglucosidase alfa on ptosis in participants with infantile-onset Pompe disease previously treated with alglucosidase alfa
S. Grace Prakalapakorn(Duke University), Priya S. Kishnani(Duke Medical Center), Satoko Kumada(Tokyo Metropolitan Neurological Hospital), Kristina An Haack(Sanofi (France)), Alexander Broomfield(St Mary's Hospital), Hirotaka Ohki(Tokyo Metropolitan Children's Medical Center), Si Houn Hahn(University of Washington), Anaïs Brassier(Hôpital Necker-Enfants Malades), Xianzhang Meng(Jilin Agricultural University), Judith Johnson(Sanofi (United States)), David Kronn(New York Medical College), Samia Pichard, Yin‐Hsiu Chien(National Taiwan University Hospital), François Labarthe(Université de Tours), James Davison(Great Ormond Street Hospital for Children NHS Foundation Trust)
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