Mini-COMET study: Individual participant-level responses to treatment in patients with infantile-onset Pompe disease receiving repeated dose regimens of avalglucosidase alfa or alglucosidase alfa who were previously treated with alglucosidase alfa
Priya S. Kishnani(Duke Medical Center), David Kronn(New York Medical College), Satoko Kumada(Tokyo Metropolitan Neurological Hospital), Kristina An Haack(Sanofi (France)), Alexander Broomfield(St Mary's Hospital), Hirotaka Ohki(Tokyo Metropolitan Children's Medical Center), Si Houn Hahn(University of Washington), Anaïs Brassier(Hôpital Necker-Enfants Malades), Xianzhang Meng(Jilin Agricultural University), Judith Johnson(Sanofi (United States)), Samia Pichard, Yin‐Hsiu Chien(National Taiwan University Hospital), François Labarthe(Université de Tours), James Davison(Great Ormond Street Hospital for Children NHS Foundation Trust)
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