Patient-customized oligonucleotide therapy for a rare genetic disease
Kim J(Boston Children's Hospital), Yu Tw(Boston Children's Hospital), Kira A. Dies(Boston Children's Hospital), Berde Cb(Boston Children's Hospital), DiDonato RL(Boston Children's Hospital), Jai Vaze(Institut thématique Génétique, génomique et bioinformatique), Snyder RO(Boston Children's Hospital), Myriam Armant(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Loes L. Cornelissen(Boston Children's Hospital), Lee Ea(Boston Children's Hospital), Annapurna Poduri(Broad Institute), Adam P. Patterson(Boston Children's Hospital), Alessandra Biffi(University of Padua), Alla V. Tsytsykova(Boston Children's Hospital), Beggs Ah, Pendergast MK(Boston Children's Hospital), Belur NR(Boston Children's Hospital), Augustine EF(Boston Children's Hospital), Goldkind SF(Boston Children's Hospital), Black LE(Boston Children's Hospital), Ashley Kuniholm(Boston Children's Hospital), Goodlett BD(Boston Children's Hospital), Amy L. Pasternak(Boston Children's Hospital), Loretta A. Williams(The University of Texas MD Anderson Cancer Center), Pflock KA(Boston Children's Hospital), Kristina Fredriksen(Northwestern University), Shu‐Hsun Chu(National Taiwan University Hospital), Riley Bl(Boston Children's Hospital), Genetti CA(Boston Children's Hospital), Park PJ(Boston Children's Hospital), Moufawad El Achkar C(Boston Children's Hospital), Kimberly Tyndall(Anna Needs Neuroblastoma Answers), Agrawal Pb(Boston Children's Hospital), P. Ellen Grant(Boston Children's Hospital), Julie Douville(Charles River Laboratories (Netherlands)), Aubrie Soucy(Institut thématique Génétique, génomique et bioinformatique), Urion DK(Boston Children's Hospital), Allison R. Larson(Georgetown University), Olaf A. Bodamer(Broad Institute), Iva Stojkovska(Northwestern University), Waisbren SE(Boston Children's Hospital), Bruce Barton(University of Massachusetts Chan Medical School), Mazzulli JR(Boston Children's Hospital), Hu Chen(Baylor College of Medicine), Charles B. Reed(Boston Children's Hospital), Berry Er(Boston Children's Hospital), Jaewoo Choi(Boston Children's Hospital), Pereira Lm(Boston Children's Hospital)
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