Patient-Customized Oligonucleotide Therapy for a Rare Genetic DiseaseJin‐Kuk Kim, Timothy W. Yu, Julie Douville et al.|New England Journal of Medicine|2019Cited by 823
Patient-customized oligonucleotide therapy for a rare genetic diseaseKim J, Yu Tw, Hu Chen et al.|Yearbook of pediatric endocrinology|2020Cited by 40