Application of N-palmitoyl-O-phosphocholineserine for diagnosis and assessment of response to treatment in Niemann-Pick type C disease
Rohini Sidhu(Washington University in St. Louis), Xuntian Jiang(Washington University in St. Louis), Jean E. Schaffer(Joslin Diabetes Center), Elizabeth Berry‐Kravis(Rush University Medical Center), Nicole Y. Farhat(Eunice Kennedy Shriver National Institute of Child Health and Human Development), Raymond Wang(Children's Hospital of Orange County), Janine Reunert(University of Münster), Charles Marques Lourenço(Universidade de São Paulo), Forbes D. Porter(National Institutes of Health), Ellen Plummer(Medford Radiology Group), Thorsten Marquardt(Klinik und Poliklinik für Kinder- und Jugendmedizin), An Dang(Eunice Kennedy Shriver National Institute of Child Health and Human Development), Olaf A. Bodamer(Broad Institute), Pamela Kell(Washington University in St. Louis), Roberto Giugliani(Universidade Federal do Rio Grande do Sul), Dennis J. Dietzen(Washington University in St. Louis), Daniel Ory(Institut de France), Charles H. Vite(University of Florida)
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