Treatment of Fabry’s Disease with the Pharmacologic Chaperone Migalastat
Dominique P. Germain(Assistance Publique – Hôpitaux de Paris), Raphael Schiffmann(Texas Christian University), William R. Wilcox(Emory University), Elizabeth Ludington(Université Paris-Saclay), Fatih Süheyl Ezgü(Gazi University), Derralynn Hughes(Royal Free London NHS Foundation Trust), Roser Torrá(Universitat Autònoma de Barcelona), Claudio Feliciani(University of Parma), John Kirk(Université Paris-Saclay), Maryam Banikazemi(University of Alabama at Birmingham), Suma P. Shankar(Emory University), Seymour Packman(University of California, San Francisco), Majed Dasouki(University of Kansas), Carrolee Barlow(Escape Therapeutics (United States)), Charles Marques Lourenço(Universidade de São Paulo), David J. Lockhart(Io Therapeutics (United States)), Usama Sharaf El Din(Université Paris-Saclay), C. Ronald Scott(University of Washington), Elfrida R. Benjamin(Université Paris-Saclay), Kathy Nicholls(Melbourne Health), Julie Yu(Hospital for Sick Children), David N. Finegold(University of Pittsburgh), Özlem Göker-Alpan(Lysosomal and Rare Disorders Research and Treatment Center), Nina Skuban(Université Paris-Saclay), Ana Jovanović(Manchester Academic Health Science Centre), Pilar Giraldo(Université Paris-Saclay), Drago Bratkovic(Women's and Children's Hospital), Daniel G. Bichet(Hôpital du Sacré-Cœur de Montréal), Ulla Feldt‐Rasmussen(Copenhagen University Hospital), Stephen Waldek, Roberto Giugliani(Universidade Federal do Rio Grande do Sul), Nicola Longo(Center for Human Genetics), Jeff Castelli(Université Paris-Saclay), Christopher Viereck(Université Paris-Saclay), Ahmad Tuffaha(University of Kansas Medical Center), Jay Barth(Université Paris-Saclay), Franklin K. Johnson(Université Paris-Saclay), Khan Nedd(Université Paris-Saclay), Joel Charrow(Northwestern University), Hernan Amartino(Université Paris-Saclay)
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