In Vivo Outcome of Homology-Directed Repair at the HBB Gene in HSC Using Alternative Donor Template Delivery Methods
Sowmya Pattabhi, David J. Rawlings(Center for Infectious Disease Research), Mason P. Berger, Christopher T. Lux, Olivier Nègre(Inserm), Andrew M. Scharenberg(CTI BioPharma (Italy)), S. N. Lotti, Calvin Lee(Bluebird Bio (United States)), Swati Singh, Kyle Jacoby
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