In Vivo Outcome of Homology-Directed Repair at the HBB Gene in HSC Using Alternative Donor Template Delivery MethodsSowmya Pattabhi, David J. Rawlings, Christopher T. Lux et al.|Molecular Therapy — Nucleic Acids|2019Cited by 96
TALEN-Mediated Gene Editing of HBG in Human Hematopoietic Stem Cells Leads to Therapeutic Fetal Hemoglobin InductionChristopher T. Lux, David J. Rawlings, Sowmya Pattabhi et al.|Molecular Therapy — Methods & Clinical Development|2018Cited by 51