Comparative Studies Reveal Robust HbF Induction By Editing of HBG1/2 Promoters or BCL11A Erythroid-Enhancer in Human CD34+ Cells but That BCL11A Erythroid-Enhancer Editing Is Associated with Selective Reduction in Erythroid Lineage Reconstitution in a Xenotransplantation ModelKai‐Hsin Chang, Haiyan Jiang, Scott Haskett et al.|Blood|2018Cited by 9
PS1518 GENOME EDITING OF HBG1/2 PROMOTER LEADS TO ROBUST HBF INDUCTION IN VIVO, WHILE EDITING OF BCL11A ERYTHROID ENHANCER RESULTS IN ERYTHROID DEFECTSJonathon Heath, Kaiwen Chang, Edouard De Dreuzy et al.|HemaSphere|2019Cited by 8