Therapeutic gene editing in CD34+ hematopoietic progenitors from Fanconi anemia patients
Begoña Díez(Centre for Biomedical Network Research on Rare Diseases), Paula Rı́o(Centre for Biomedical Network Research on Rare Diseases), Giulia Schiroli(Xperi (United States)), Pietro Genovese(Boston Children's Hospital), Angelo Lombardo(Vita-Salute San Raffaele University), Laura Ugalde(Centre for Biomedical Network Research on Rare Diseases), Francisco J Roman‐Rodriguez(Centre for Biomedical Network Research on Rare Diseases), Cristina Díaz de Heredia(Universitat Autònoma de Barcelona), Julián Sevilla(University of Southern Denmark), Sandra Rodríguez(Spanish National Cancer Research Centre), Luigi Naldini(Vita-Salute San Raffaele University), Lara Álvarez(Centre for Biomedical Network Research on Rare Diseases), Michael C. Holmes(Somerville Hospital), Juan A. Bueren(Centro de Investigación Biomédica en Red)
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