Therapeutic gene editing in CD34+ hematopoietic progenitors from Fanconi anemia patientsBegoña Díez, Paula Rı́o, Lara Álvarez et al.|EMBO Molecular Medicine|2017Cited by 61
Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trialsPaula Rı́o, Josune Zubicaray, Susana Navarro et al.|The Lancet|2024Cited by 27