Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Craig M. McDonald(University of California Davis Medical Center), Craig Campbell(Western University), Ricardo Erazo Torricelli(Hospital Luis Calvo Mackenna), Richard S. Finkel(Children's Hospital of Philadelphia), Kevin M. Flanigan(Nationwide Children's Hospital), Nathalie Goemans(KU Leuven), Peter Heydemann(Rush University Medical Center), Anna Kamińska(Medical University of Warsaw), Janbernd Kirschner(University of Freiburg), Francesco Muntoni(Great Ormond Street Hospital), A. Nascimento Osorio(Hospital Sant Joan de Déu Barcelona), Ulrike Schara(University of Duisburg-Essen), Thomas Sejersen(Karolinska University Hospital), Perry B. Shieh(University of California, Los Angeles), H. Lee Sweeney(University of Florida), Haluk Topaloğlu(Hacettepe University Hospital), M. Tulinius(Drottning Silvias barn- och ungdomssjukhus), Juan J. Vílchez(Hospital Universitari i Politècnic La Fe), Thomas Voït(Great Ormond Street Hospital), Brenda Wong(Cincinnati Children's Hospital Medical Center), Gary Elfring(PTC Therapeutics (United States)), Hans Kröger(PTC Therapeutics (United States)), Xiaohui Luo(PTC Therapeutics (United States)), Joseph McIntosh(PTC Therapeutics (United States)), Tuyen Ong(PTC Therapeutics (United States)), Peter Riebling(PTC Therapeutics (United States)), Marcio Ferreira de Souza(PTC Therapeutics (United States)), Robert J. Spiegel(PTC Therapeutics (United States)), Stuart W. Peltz(PTC Therapeutics (United States)), Eugenio Mercuri(Università Cattolica del Sacro Cuore), Lindsay N. Alfano, Michelle Eagle, M. James, Linda Lowes, Anna Mayhew(Medical University of Warsaw), Elena Mazzone, Leslie Nelson, Kristy Rose, Hoda Abdel‐Hamid, Susan Apkon, Richard J. Barohn, Enrico Bertini, Clemens Bloetzer, Lausanne Canton de Vaud, Russell J. Butterfield, B. Chabrol, Jong‐Hee Chae, Daehak-ro Jongno-gu, Giacomi Pietro Comi, Basil T. Darras, Jahannaz Dastgir, Isabelle Desguerre, Raúl G. Escobar, Erika Finanger, Michela Guglieri, Imelda Hughes, Susan T. Iannaccone, Kristi Jones, Peter Karachunski(PTC Therapeutics (United States)), Martin Kudr, Timothy Lotze, Jean K. Mah, Katherine D. Mathews, Yoram Nevo, Julie Parsons, Yann Péréon, Alexandra Prufer de Queiroz Campos Araújo, J. Ben Renfroe, Maria Bernadete Dutra de Resende, Monique M. Ryan, Kathryn Selby, Gihan Tennekoon, Giuseppe Vita
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