Functional changes in Duchenne muscular dystrophyElena Mazzone, Eugenio Mercuri, Gessica Vasco et al.|Neurology|2011Cited by 178
Hammersmith Functional Motor Scale and Motor Function Measure-20 in non ambulant SMA patientsElena Mazzone, Eugenio Mercuri, Rita De Sanctis et al.|Neuromuscular Disorders|2014Cited by 64
Six minute walk test in type III spinal muscular atrophy: A 12 month longitudinal studyElena Mazzone, Eugenio Mercuri, F. Bianco et al.|Neuromuscular Disorders|2013Cited by 60
Safety and efficacy of apitegromab in nonambulatory type 2 or type 3 spinal muscular atrophy (SAPPHIRE): a phase 3, double-blind, randomised, placebo-controlled trialThomas O. Crawford, Barbara Steinborn, Marta Gómez García de la Banda et al.|The Lancet Neurology|2025Cited by 22
Revised North Star ambulatory assessment for young boys with Duchenne muscular dystrophyEugenio Mercuri, Marika Pane, Giorgia Coratti et al.|Neuromuscular Disorders|2016Cited by 3