Clinical efficacy of gene-modified stem cells in adenosine deaminase–deficient immunodeficiency

Kit L. Shaw(Boston Children's Hospital), Donald B. Kohn(University of California, Los Angeles), Alejandra Davila(University of California, Los Angeles), Suparna Mishra(University of California, Los Angeles), Sabine Geiger(Christian Doppler Klinik), Michael S. Hershfield(Duke University), Suzanne Skoda‐Smith(University of Washington), Denise A. Carbonaro(University of California, Los Angeles), Allen Chi-Shing Yu(deCODE Genetics (Iceland)), Sally Shupien(Takeda (United States)), Satiro De Oliveira(University of California, Los Angeles), Aaron Cooper(Memorial Sloan Kettering Cancer Center), Roshini S. Abraham(Nationwide Children's Hospital), Arumugam Balamurugan(University of California, Los Angeles), Beatriz Campo Fernandez(Erciyes University), Greg M. Podsakoff(Children's Hospital of Los Angeles), David Buchbinder(Children's Hospital of Orange County), Theodore B. Moore(University of California, Los Angeles), Christopher Silvin(National Human Genome Research Institute), Barbara C. Engel(Children's Hospital of Philadelphia), Alan K. Ikeda(Baxalta (United States)), Fabio Candotti(Institute of Immunology), Otto O. Yang(University of California, Los Angeles), Andrew M. Scharenberg(CTI BioPharma (Italy)), David W. Gjertson(University of California, Los Angeles), Yeong Choi(University of California, Los Angeles), G. Jayashree Jagadeesh(National Human Genome Research Institute), Barbara Nowicki(Ronald Reagan UCLA Medical Center), Ken Purdy(Kaiser Permanente Santa Clara Medical Center), Linda Muul(National Human Genome Research Institute), Elizabeth Garabedian(National Human Genome Research Institute), E Smogorzewska(Children's Hospital of Los Angeles), Kenneth Cornetta(Indiana University – Purdue University Indianapolis), Neena Kapoor(University of Southern California), John Tse(Ronald Reagan UCLA Medical Center), Stacie M. Anderson(National Institutes of Health), Berkley Brown(University of California, Los Angeles), Provaboti Barman(University of California, Los Angeles), Pei-Yu Fu(University of California, Los Angeles), Dayna Terrazas(Erciyes University), K. Mohan(University of Washington), Radha Rishi(Allergy Associates Research Center), Xiaoyan Wang(University of California, Los Angeles), Robert Sokolic(National Human Genome Research Institute)
Journal of Clinical Investigation
March 26, 2017
Cited by 81


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