Gene therapy comes of age
Cynthia E. Dunbar(National Institutes of Health), Michel Sadelain(Memorial Sloan Kettering Cancer Center), J. Keith Joung(Massachusetts General Hospital), Donald B. Kohn(University of California, Los Angeles), Katherine A. High(Children's Hospital of Philadelphia), Keiya Ozawa(Jichi Medical University)
Cited by 1,354
Related Papers
High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells
|Nature Biotechnology|2013|3.3k
CRISPR-Cas systems for editing, regulating and targeting genomes
|Nature Biotechnology|2014|3.2k
Efficient genome editing in zebrafish using a CRISPR-Cas system
|Nature Biotechnology|2013|3k
High-fidelity CRISPR–Cas9 nucleases with no detectable genome-wide off-target effects
|Nature|2016|2.7k
Efficacy and Toxicity Management of 19-28z CAR T Cell Therapy in B Cell Acute Lymphoblastic Leukemia
|Science Translational Medicine|2014|2.5k