Follistatin Gene Therapy for Sporadic Inclusion Body Myositis Improves Functional Outcomes

Jerry R. Mendell(Nationwide Children's Hospital), Zarife Sahenk(Nationwide Children's Hospital), Samiah Al-Zaidy(Nationwide Children's Hospital), Louise R. Rodino‐Klapac(Nationwide Children's Hospital), Linda Lowes(Nationwide Children's Hospital), Lindsay N. Alfano(Nationwide Children's Hospital), Katherine Berry(Nationwide Children's Hospital), N. Miller(Nationwide Children's Hospital), Mehmet E. Yalvaç(Nationwide Children's Hospital), Igor Dvorchik(Nationwide Children's Hospital), Melissa Moore‐Clingenpeel(Nationwide Children's Hospital), Kevin M. Flanigan(Nationwide Children's Hospital), Kathleen Church(Nationwide Children's Hospital), Kim Shontz(Nationwide Children's Hospital), Choumpree Curry(Nationwide Children's Hospital), Sarah Lewis(Nationwide Children's Hospital), Markus McColly(Nationwide Children's Hospital), Mark Hogan(Nationwide Children's Hospital), Brian K. Kaspar(Nationwide Children's Hospital)
Molecular Therapy
March 7, 2017
Cited by 105Open Access
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