Adeno-Associated Virus-Based Gene Therapy for CNS DiseasesMichaël Hocquemiller, Nathalie Cartier(Université Paris-Sud)Human Gene TherapyJune 8, 201610.1089/hum.2016.087Cited by 283SaveCiteExport RISWatch citationsRelated PapersHematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy|Science|2009|1.5kTransfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia|Nature|2010|1.3k