Long-term Correction of Very Long-chain Acyl-CoA Dehydrogenase Deficiency in Mice Using AAV9 Gene Therapy
Allison M. Keeler(University of Massachusetts Chan Medical School), Terence R. Flotte(University of Massachusetts Chan Medical School), Thomas J. Conlon(Adelson Foundation), Travis Cossette(University of Florida), Qiushi Tang(Chinese Journal of Integrated Traditional and Western Medicine), Glenn A. Walter(University of Florida), Kirsten Erger(University of Florida), Fu Dungtao(University of Florida), Christian Mueller(AbbVie (Germany)), Huadong Zeng(University of Florida), Scott A. Shaffer(University of Massachusetts Chan Medical School)
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