728. Safety and Bioactivity of rAAV2-hAAT in alpha-1 Antitrypsin-Deficient Patients in a Phase I Clinical Trial
Mark Brantly(University of Florida), Terence R. Flotte(University of Massachusetts Chan Medical School), Richard O. Snyder(Inserm), Sihong Song(American Association of Colleges of Pharmacy), Thomas J. Conlon(Adelson Foundation), Margaret Humphries(University of Massachusetts Chan Medical School), Barry J. Byrne(University of Florida), Terry Spencer(Boston Children's Museum), Carolyn T. Spencer(University of Florida)
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