Cystic fibrosis newborn screening: using experience to optimize the screening algorithmJaime E. Hale, Anne Marie Comeau, Allen Lapey et al.|Journal of Inherited Metabolic Disease|2010Cited by 21
728. Safety and Bioactivity of rAAV2-hAAT in alpha-1 Antitrypsin-Deficient Patients in a Phase I Clinical TrialMark Brantly, Terence R. Flotte, Terry Spencer et al.|Molecular Therapy|2006Cited by 0