Hurdles in treating Hurler disease: potential routes to achieve a “real” cureBrigitte T. A. van den Broek, Peter M. van Hasselt, Caroline A. Lindemans et al.|Blood Advances|2020Cited by 16
Long-term effect of hematopoietic cell transplantation on systemic inflammation in patients with mucopolysaccharidosesBrigitte T. A. van den Broek, Stefan Nierkens, Caroline A. Lindemans et al.|Blood Advances|2021Cited by 8