Hurdles in treating Hurler disease: potential routes to achieve a “real” cure
Brigitte T. A. van den Broek(University Medical Center Utrecht), Peter M. van Hasselt(Utrecht University), Caroline A. Lindemans(University Medical Center Utrecht), Nanda M. Verhoeven‐Duif(University Medical Center Utrecht), Stefan Nierkens(Utrecht University), Jaap Jan Boelens(Wilhelmina Children's Hospital), Jaap van Doorn, Charlotte V. Hegeman
Cited by 16
Related Papers
Gut microbiome–derived metabolites modulate intestinal epithelial cell damage and mitigate graft-versus-host disease
|Nature Immunology|2016|727
Early cytomegalovirus reactivation remains associated with increased transplant-related mortality in the current era: a CIBMTR analysis
|Blood|2016|554