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Adult Hemoglobin Production, Chain Rebalance, and Splice Correction in IVS2-745 Beta-Thalassemia Patient Cells Using 2'-O-Methoxyethyl Splice-Switching OligosAlisa Dong, Stefano Rivella, Valentina Ghiaccio et al.|Blood|2016Cited by 0
2'-O-Methoxyethyl Splice-Switching Oligos to Reverse Splicing from IVS2-745 β-Thalassemia Patient Cells: A Foundation for Potential TherapiesValentina Ghiaccio, Laura Breda, Alisa Dong et al.|Blood|2019Cited by 0