In vivo hematopoietic stem cell modification by mRNA deliveryLaura Breda, Hamideh Parhiz, Tyler E. Papp et al.|Science|2023Cited by 321
Forced chromatin looping raises fetal hemoglobin in adult sickle cells to higher levels than pharmacologic inducersLaura Breda, Stefano Rivella, Irene Motta et al.|Blood|2016Cited by 83
Lentiviral vector ALS20 yields high hemoglobin levels with low genomic integrations for treatment of beta-globinopathiesLaura Breda, Stefano Rivella, Valentina Ghiaccio et al.|Molecular Therapy|2021Cited by 23
Use of HSC-targeted LNP to generate a mouse model of lethal α-thalassemia and treatment via lentiviral gene therapyMaxwell Chappell, Stefano Rivella, Laura Breda et al.|Blood|2024Cited by 11
Inclusion of a short hairpin RNA targeting <i>BCL11A</i> into a β-globin expressing vector allows concurrent synthesis of curative adult and fetal hemoglobinSílvia Pires Lourenço, Stefano Rivella, Danuta Jarocha et al.|Haematologica|2021Cited by 10