Multi-targeting zinc finger nuclease vector unsilences paternal UBE3A in a mouse model of Angelman syndromeHannah Bazick, Mark J. Zylka|Gene Therapy|2025Cited by 4
Nickase NmCas9 unsilences paternal Ube3a in a mouse model of Angelman syndrome without causing AAV vector integrationHannah Bazick, Mark J. Zylka|Scientific Reports|2026Cited by 0