Nickase NmCas9 unsilences paternal Ube3a in a mouse model of Angelman syndrome without causing AAV vector integrationHannah Bazick(University of North Carolina at Chapel Hill), Mark J. Zylka(University of North Carolina at Chapel Hill)Scientific ReportsMay 14, 202610.1038/s41598-026-52498-4Cited by 0SaveCiteExport RISWatch citationsRelated PapersMulti-targeting zinc finger nuclease vector unsilences paternal UBE3A in a mouse model of Angelman syndrome|Gene Therapy|2025|4