The Mini-COMET Clinical Trial: Safety and Efficacy of Avalglucosidase Alfa after 97 Weeks of Treatment in Children with Infantile-Onset Pompe Disease Previously Treated with Alglucosidase Alfa
David Kronn(New York Medical College), Catherine Wilson(Murdoch Children's Research Institute), S. Grace Prakalapakorn(Duke University), James Davison(Great Ormond Street Hospital for Children NHS Foundation Trust), Satoko Kumada(Tokyo Metropolitan Neurological Hospital), Swathi Tammireddy, Kristina An Haack(Sanofi (France)), Alexander Broomfield(St Mary's Hospital), Hirotaka Ohki(Tokyo Metropolitan Children's Medical Center), Olivier Huynh‐Ba(Sanofi (France)), Susan Sparks(Children's National), Si Houn Hahn(University of Washington), Anaïs Brassier(Hôpital Necker-Enfants Malades), Tianyue Zhou, Susan Richards(MRC Clinical Trials Unit at UCL), Yin‐Hsiu Chien(National Taiwan University Hospital), François Labarthe(Université de Tours)
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