CRISPR/Cas9-mediated generation of a <i>de novo C9ORF72</i> knock-in isogenic iPSC cell bank to model ALS and FTDNiamh L. O’Brien, Sarah Mizielinska|bioRxiv (Cold Spring Harbor Laboratory)|2025Cited by 0
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C9ORF72-derived polyGR polypeptides disrupt passive nucleocytoplasmic transport by tuning protein affinity for the nuclear pore barrierDaniel A. Solomon, Sarah Mizielinska|bioRxiv (Cold Spring Harbor Laboratory)|2026Cited by 0