CRISPR/Cas9-mediated generation of a <i>de novo C9ORF72</i> knock-in isogenic iPSC cell bank to model ALS and FTD

Niamh L. O’Brien(King's College London), Sarah Mizielinska(King's College London)
bioRxiv (Cold Spring Harbor Laboratory)
November 13, 2025
Cited by 0


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