2'-O-methoxyethyl splice-switching oligos correct splicing from IVS2-745 β-thalassemia patient cells restoring HbA production and chain rebalanceAlisa Dong, Laura Breda, Andy Watt et al.|Haematologica|2020Cited by 2
Adult Hemoglobin Production, Chain Rebalance, and Splice Correction in IVS2-745 Beta-Thalassemia Patient Cells Using 2'-O-Methoxyethyl Splice-Switching OligosAlisa Dong, Stefano Rivella, Valentina Ghiaccio et al.|Blood|2016Cited by 0
2'-O-Methoxyethyl Splice-Switching Oligos to Reverse Splicing from IVS2-745 β-Thalassemia Patient Cells: A Foundation for Potential TherapiesValentina Ghiaccio, Laura Breda, Alisa Dong et al.|Blood|2019Cited by 0