In Vivo Assessment of Potential Therapeutic Approaches for USH2A-Associated DiseasesNachiket Pendse, Qin Liu, Morgan L. Maeder et al.|Advances in experimental medicine and biology|2019Cited by 32
Ift172 conditional knock-out mice exhibit rapid retinal degeneration and protein trafficking defectsPriya Gupta, Kinga M. Bujakowska, Nachiket Pendse et al.|Human Molecular Genetics|2018Cited by 29
Systematic empirical evaluation of individual base editing targets: Validating therapeutic targets in USH2A and comparison of methodsYuki Tachida, Jason Comander, Kannan Vrindavan Manian et al.|Molecular Therapy|2025Cited by 11
Exon 13-skipped USH2A protein retains functional integrity in mice, suggesting an exo-skipping therapeutic approach to treat USH2A-associated diseaseNachiket Pendse, Qin Liu, Zheng‐Yi Chen et al.|bioRxiv (Cold Spring Harbor Laboratory)|2020Cited by 9