In Vivo Assessment of Potential Therapeutic Approaches for USH2A-Associated Diseases
Nachiket Pendse(Massachusetts Eye and Ear Infirmary), Qin Liu(Massachusetts Eye and Ear Infirmary), Verónica Lamas(Massachusetts Eye and Ear Infirmary), Zheng‐Yi Chen(Massachusetts Eye and Ear Infirmary), Basil S. Pawlyk(Berman Center for Outcomes and Clinical Research), Morgan L. Maeder(Editas Medicine (United States)), Eric A. Pierce(Broad Institute)
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