Antisense Proline-Arginine RAN Dipeptides Linked to C9ORF72-ALS/FTD Form Toxic Nuclear Aggregates that Initiate In Vitro and In Vivo Neuronal DeathXinmei Wen, Davide Trotti, Thomas Westergard et al.|Neuron|2014Cited by 556
PIKFYVE inhibition mitigates disease in models of diverse forms of ALSShu‐Ting Hung, Justin K. Ichida|Cell|2023Cited by 97
Identification and therapeutic rescue of autophagosome and glutamate receptor defects in C9ORF72 and sporadic ALS neuronsYingxiao Shi, Justin K. Ichida|JCI Insight|2019Cited by 60