Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic DiseaseKiran Musunuru, Rebecca C. Ahrens‐Nicklas, Julia Hacker et al.|New England Journal of Medicine|2025Cited by 272
Efficient in vivo base editing via single adeno-associated viruses with size-optimized genomes encoding compact adenine base editorsJessie R. Davis, David R. Liu, Xiao Wang et al.|Nature Biomedical Engineering|2022Cited by 186
Publisher Correction: Efficient in vivo base editing via single adenoassociated viruses with size-optimized genomes encoding compact adenine base editorsJessie R. Davis, David R. Liu, Isaac P. Witte et al.|Nature Biomedical Engineering|2022Cited by 4