Efficient in vivo base editing via single adeno-associated viruses with size-optimized genomes encoding compact adenine base editors
Jessie R. Davis(Broad Institute), David R. Liu(Broad Institute), Kiran Musunuru(University of Pennsylvania), Isaac P. Witte(Broad Institute), Samagya Banskota(Broad Institute), Tony P. Huang(Broad Institute), Nabil G. Seidah(Montreal Clinical Research Institute), Aditya Raguram(Broad Institute), Xiao Wang(University of Pennsylvania), Jonathan M. Levy(Broad Institute)
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