CRISPR-based gene editing enables <i>FOXP3</i> gene repair in IPEX patient cellsMarianne Goodwin, Rosa Bacchetta, Federica Barzaghi et al.|Science Advances|2020Cited by 113
Human‐engineered Treg‐like cells suppress FOXP3‐deficient T cells but preserve adaptive immune responses <i>in vivo</i>Yohei Sato, Rosa Bacchetta, Laura Passerini et al.|Clinical & Translational Immunology|2020Cited by 54