CRISPR-based gene editing enables <i>FOXP3</i> gene repair in IPEX patient cells
Marianne Goodwin(Stanford University), Rosa Bacchetta(Lucile Packard Children's Hospital), Mara Pavel-Dinu(Stanford University), Maria Garcia-Lloret(University of California, Los Angeles), Uma Lakshmanan(Stanford University), Suzette Shipp(Stanford University), Mansi Narula(Stanford University), Ciaran M. Lee(University College Cork), Manish J. Butte(University of California, Los Angeles), Gang Bao(Tianjin Stomatological Hospital), Ami J. Shah(University of California, Los Angeles), Alice Bertaina(Stanford University), Federica Barzaghi(The San Raffaele Telethon Institute for Gene Therapy), Ayal Hendel(Gladstone Institutes), Adam Sheikali(Stanford University), Luise Froessl(Stanford University), Cindy S. Bauer(Phoenix Children's Hospital), Laura Passerini(The San Raffaele Telethon Institute for Gene Therapy), Matthew H. Porteus(Lucile Packard Children's Hospital), Maria‐Grazia Roncarolo(Vita-Salute San Raffaele University), Holly Miller(Phoenix Children's Hospital)
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