Surprises of genetic engineeringNina Raben, Paul H. Plötz, M. J. Danon et al.|Neurology|2001Cited by 105
Glycogen Stored in Skeletal but Not in Cardiac Muscle in Acid α-Glucosidase Mutant (Pompe) Mice Is Highly Resistant to Transgene-Encoded Human EnzymeNina Raben, Paul H. Plötz, Alicia Lee et al.|Molecular Therapy|2002Cited by 60
Glycogen Stored in Skeletal but Not in Cardiac Muscle in Acid α-Glucosidase Mutant (Pompe) Mice Is Highly Resistant to Transgene-Encoded Human EnzymeNina Raben, Paul H. Plötz, Tejas Jatkar et al.|Molecular Therapy|2002Cited by 58
Induction of Tolerance to a Recombinant Human Enzyme, Acid Alpha-Glucosidase, in Enzyme Deficient Knockout MiceNina Raben, Paul H. Plötz, Alicia Lee et al.|Transgenic Research|2003Cited by 32
Transcriptional Regulation of the Human Acid α-Glucosidase GeneBo Yan, Paul H. Plötz, Joris J. Heus et al.|Journal of Biological Chemistry|2001Cited by 18