Glycogen Stored in Skeletal but Not in Cardiac Muscle in Acid α-Glucosidase Mutant (Pompe) Mice Is Highly Resistant to Transgene-Encoded Human Enzyme

Nina Raben(APT Therapeutics (United States)), Paul H. Plötz(National Institutes of Health), Kanneboyina Nagaraju(Children's National), Alicia Lee(National Institutes of Health), Tejas Jatkar(National Institute of Arthritis and Musculoskeletal and Skin Diseases), Nina Lu(National Institute of Arthritis and Musculoskeletal and Skin Diseases), Sunita Dwivedi(National Institute of Arthritis and Musculoskeletal and Skin Diseases)
Molecular Therapy
November 1, 2002
Cited by 60


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