Glycogen Stored in Skeletal but Not in Cardiac Muscle in Acid α-Glucosidase Mutant (Pompe) Mice Is Highly Resistant to Transgene-Encoded Human Enzyme

Nina Raben(APT Therapeutics (United States)), Paul H. Plötz(National Institutes of Health), Tejas Jatkar(National Institute of Arthritis and Musculoskeletal and Skin Diseases), Nina Lu(National Institute of Arthritis and Musculoskeletal and Skin Diseases), A LEE(National Institutes of Health), S DWIVEDI(National Institute of Arthritis and Musculoskeletal and Skin Diseases), K. Nagaraju(National Institutes of Health)
Molecular Therapy
October 28, 2002
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