Alpelisib administration reduced lymphatic malformations in a mouse model and in patientsFlorence Delestre, Guillaume Canaud, Vahid Asnafi et al.|Science Translational Medicine|2021Cited by 92
Sotorasib for Vascular Malformations Associated with <i>KRAS</i> G12C MutationAntoine Fraissenon, Guillaume Canaud, Charles Bayard et al.|New England Journal of Medicine|2024Cited by 38
PIK3CA gain-of-function mutation in adipose tissue induces metabolic reprogramming with Warburg-like effect and severe endocrine disruptionSophia Ladraa, Guillaume Canaud, Lola Zerbib et al.|Science Advances|2022Cited by 33
Targeted therapy for capillary-venous malformationsLola Zerbib, Guillaume Canaud, Sophia Ladraa et al.|Signal Transduction and Targeted Therapy|2024Cited by 28
Hemifacial myohyperplasia is due to somatic muscular PIK3CA gain-of-function mutations and responds to pharmacological inhibitionCharles Bayard, Guillaume Canaud, E. Segna et al.|The Journal of Experimental Medicine|2023Cited by 12