Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension studyDavid Adams, Michael Polydefkis, Alejandra González‐Duarte et al.|The Lancet Neurology|2020Cited by 160
Clinical and Paraclinical Indicators of Motor System Impairment in Hereditary Spastic Paraplegia: A Pilot StudyAndrea Martinuzzi, Maria Teresa Bassi, Domenico Montanaro et al.|PLoS ONE|2016Cited by 43
Five-Year Results With Patisiran for Hereditary Transthyretin Amyloidosis With PolyneuropathyDavid Adams, Mónica Freitas, Jonas Wixner et al.|JAMA Neurology|2025Cited by 34
The role of ethnicity and native-country income in multiple sclerosis: the Italian multicentre study (MS-MigIT)Alessia Bianchi, Domenica Matranga, Francesco Patti et al.|Journal of Neurology|2024Cited by 2
Diagnostic and therapeutic approaches of mixed cryoglobulinemia in PITER (Piattaforma Italiana per lo studio della Terapia delle Epatiti viRali) cohortLoreta A. Kondili, Anna Linda Zignego, M. Vinci et al.|Journal of Hepatology|2017Cited by 1