Five-Year Results With Patisiran for Hereditary Transthyretin Amyloidosis With Polyneuropathy
David Adams(Mount Sinai Health System), Mónica Freitas, Annie Verschueren(Aix-Marseille Université), James A. R. Dalton(Universitat Autònoma de Barcelona), Jonas Wixner(Umeå University), John L. Berk(Boston University), Massimo Russo, Vincent Lau(University of Alberta), Michelle Kaku(Icahn School of Medicine at Mount Sinai), Kátia Valdrez, Janice F. Wiesman(Boston University), Carlos Marques‐Neves, Aude‐Marie Grapperon, Javier Martínez Pérez(Hospital de Santo António), Cristina Alves(Centro Hospitalar do Porto), Luca Gentile, Elena Yureneva(British Heart Foundation), Julia R Monte(Centro Hospitalar do Porto), Mitsuharu Ueda(Kumamoto University), Miguel Oliveira Santos(Centro Hospitalar Lisboa Norte), Émilien Delmont(Assistance Publique Hôpitaux de Marseille), Isabel Conceição(Université Paris-Sud), Nuno Correia, Laura Obici(University of Pavia), Catarina Falcão de Campos, Amanda Peltier, Anna Mazzeo(University of Messina), Márcio Cardoso(Centro Hospitalar Lisboa Norte), Kelley E. Capocelli(Children's Hospital Colorado), Michael Polydefkis(Université Paris-Sud), Inês Cardoso, Marta Novais, Shahram Attarian(Aix-Marseille Université), Conceição de Azevedo Coutinho, Patrick Y. Jay(Washington University in St. Louis), Teresa Coelho(Administração Regional de Saúde de Lisboa e Vale do Tejo), Jean Pouget, Antonio Hipólito Reis(The Royal Free Hospital), John J. May(University of Kansas Medical Center), Douglas DeLong, Shaun Bender(Alnylam Pharmaceuticals (United States)), Angela Dispenzieri(Mayo Clinic), Nádia Guimarães, Vincenzo Rizzo
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