Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study
David Adams(Mount Sinai Health System), Vincenzo Rizzo, Annie Verschueren(Aix-Marseille Université), Marianne T. Sweetser(Alnylam Pharmaceuticals (United States)), Theodoros Kyriakides(University of Nicosia), James A. R. Dalton(Universitat Autònoma de Barcelona), Dianna Quan(University of Michigan), Giuseppe Vita(University of Messina), Jonas Wixner(Umeå University), John L. Berk(Boston University), Hartmut Schmidt(Université Paris-Sud), Luca Gentile(University of Messina), Massimo Russo, Márcia Waddington‐Cruz(Université Paris-Sud), Janice F. Wiesman(Boston University), Jennifer Victory, Aude‐Marie Grapperon, Jing Jing Wang(Trinity College Dublin), Emre Aldinc(Alnylam Pharmaceuticals (United States)), Violaine Planté‐Bordeneuve(Université Paris-Est Créteil), Mitsuharu Ueda(Kumamoto University), Erhan Berber(Alnylam Pharmaceuticals (United States)), Julian D. Gillmore(Alnylam Pharmaceuticals (United States)), Matthew T. White(Alnylam Pharmaceuticals (United States)), Émilien Delmont(Assistance Publique Hôpitaux de Marseille), Senda Ajroud‐Driss, Thomas H. Brannagan(Columbia University), Isabel Conceição(Université Paris-Sud), Arnt V. Kristen(Heidelberg University), Catherine Gilmore(Victoria Hospital), Anna Mazzeo(University of Messina), Alejandra González‐Duarte(NYU Langone Health), Michael Polydefkis(Université Paris-Sud), Shahram Attarian(Aix-Marseille Université), Caitlin Brueckner, Teresa Coelho(Universidade do Porto), Inés Asunción Losada López(Health Research Institute of the Balearic Islands), Jean Pouget, Michelle M. Mezei(Université Paris-Sud), John J. May(University of Kansas Medical Center), Douglas DeLong, Elizabeth A. Mauricio(WinnMed), Victoria Lazzari, Michel Slama(Université Paris Cité), Angela Dispenzieri(Mayo Clinic), Saran Diallo
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