European expert recommendations for comprehensive pre-treatment, treatment-phase and post-treatment care of patients with metachromatic leukodystrophy treated with autologous haematopoietic stem and progenitor cell gene therapy

Lucia Laugwitz(University Children's Hospital Tübingen), Valeria Calbi(IRCCS Ospedale San Raffaele), Katharina Wehner(University Children's Hospital Tübingen), Jean‐Hugues Dalle(Inserm), Ingo Müller(Universität Hamburg), Dominik Turkiewicz(Skåne University Hospital), Ursula Holzer(University Children's Hospital Tübingen), Nicole I. Wolf(Emma Kinderziekenhuis), Michaela Döring(University Children's Hospital Tübingen), Pascal Martin(Hertie Institute for Clinical Brain Research), Arunabha Ghosh(St Mary's Hospital), Jan Marco Kern(University Children's Hospital Tübingen), Irene Steiner-Wilke(University Children's Hospital Tübingen), Caroline Sevin(Bicêtre Hospital), Alejandra Darling(Hospital Sant Joan de Déu Barcelona), Samuel Groeschel(University of Tübingen), Claire Horgan(Manchester University NHS Foundation Trust), Erik A. Eklund(Lund University), Nadja Kaiser(University Children's Hospital Tübingen), Dipak Ram(Royal Manchester Children's Hospital), Francesca Fumagalli(Vita-Salute San Raffaele University), Christiane Kehrer(University Children's Hospital Tübingen), Elise Yazbeck(Université Paris-Saclay), Markus Weitz(University Children's Hospital Tübingen), Julia Marsal Ricoma(Hospital Sant Joan de Déu Barcelona), Peter Lang(University Children's Hospital Tübingen), Tom Launer(University Children's Hospital Tübingen), Philipp Juengling(University Children's Hospital Tübingen), Caroline Lindemans(Princess Máxima Center), Johannes H. Schulte(University Children's Hospital Tübingen), Hendrik Rosewich(University Children's Hospital Tübingen), Annette Bley(Universität Hamburg), Maria Forsgren(Lund University)
European Journal of Paediatric Neurology
June 30, 2026
Cited by 1


Related Papers