Selection of Human Hematopoietic Stem Cells Bearing the Intended Functional Edit by Transient AND-Gate Reporters

Martina Fiumara(The San Raffaele Telethon Institute for Gene Therapy), Luigi Naldini(IRCCS Ospedale San Raffaele), Samuele Ferrari(Vita-Salute San Raffaele University), Daniele Canarutto(Vita-Salute San Raffaele University)
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June 3, 2026
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