Unbiased assessment of genome integrity and purging of adverse outcomes at the target locus upon editing of <scp> CD4 <sup>+</sup> </scp> T‐cells for the treatment of Hyper <scp>IgM1</scp>
Daniele Canarutto(Vita-Salute San Raffaele University), Luigi Naldini(Vita-Salute San Raffaele University), Ilaria Visigalli(The San Raffaele Telethon Institute for Gene Therapy), Samuele Ferrari(Vita-Salute San Raffaele University), Andrea Finocchi(Bambino Gesù Children's Hospital), Claudia Asperti(The San Raffaele Telethon Institute for Gene Therapy), Angelica Varesi(The San Raffaele Telethon Institute for Gene Therapy), Valentina Vavassori(FVA New Media Research (Italy)), Marianna Paulis(Humanitas University), Vassilios Lougaris(University of Brescia), Aurélien Jacob(The San Raffaele Telethon Institute for Gene Therapy), Simona Porcellini(The San Raffaele Telethon Institute for Gene Therapy), Luis Ignacio González‐Granado(Research Institute Hospital 12 de Octubre), Marina Radrizzani(The San Raffaele Telethon Institute for Gene Therapy), Anna Villa(Institute of Genetic and Biomedical Research), Elisabetta Rovelli(The San Raffaele Telethon Institute for Gene Therapy), Francesca Ferrua(Vita-Salute San Raffaele University), Lucia Sergi Sergi(The San Raffaele Telethon Institute for Gene Therapy), Martina Fiumara(The San Raffaele Telethon Institute for Gene Therapy)
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